Mocravimod as Adjunctive and Maintenance Treatment in AML Patients Undergoing Allo-HCT

Purpose

This is a multi-center, randomized, double-blinded, placebo controlled trial.

Condition

  • Adult Acute Myeloid Leukemia

Eligibility

Eligible Ages
Between 18 Years and 75 Years
Eligible Sex
All
Accepts Healthy Volunteers
No

Inclusion Criteria

  • Diagnosis of AML (excluding acute promyelocytic leukemia) according to the WHO 2022 classification of AML and related precursor neoplasm, including AML with myelodysplasia-related gene mutations - European Leukemia Net (ELN) high-risk or intermediate-risk AML in CR1, or AML of any risk in CR2, [CRi] is also allowable - Planned allogeneic HCT from fully matched related or unrelated donor with no more than 1 antigen mismatch or planned use of haploidentical donor using PBSC graft - Any conditioning regimen with a Transplant Conditioning Score (TCI) ≥ 1.5 - Planned use of TAC-based GvHD prophylaxis - age ≥ 18 years and ≤ 75 years - Eastern Cooperative Oncology Group (ECOG) performance status of 0 or 1

Exclusion Criteria

  • Use of CsA, anti-thymocyte globulin (ATG), alemtuzumab, abatacept for GvHD prophylaxis - Diagnosis of macular edema during screening - Cardiac/pulmonary/hepatic/renal dysfunction - Hepatic dysfunction as defined by aspartate aminotransferase (AST) and/or alanine aminotransferase (ALT) > 2.5 x upper limit of normal (ULN); or total bilirubin > 1.5 mg/dL - Renal dysfunction with estimated creatinine clearance < 45 mL/min by the Cockcroft-Gault formula - Diabetes mellitus - History or presence of uveitis at screening - History or diagnosis of macular edema

Study Design

Phase
Phase 3
Study Type
Interventional
Allocation
Randomized
Intervention Model
Parallel Assignment
Intervention Model Description
prospective, multicenter, randomized, double-blind, placebo-controlled, and 3-arm parallel group study
Primary Purpose
Treatment
Masking
Quadruple (Participant, Care Provider, Investigator, Outcomes Assessor)

Arm Groups

ArmDescriptionAssigned Intervention
Experimental
3mg mocravimod arm
3 mg of mocravimod orally once per day for 12 months
  • Drug: mocravimod
    S1PR modulator
Experimental
1mg mocravimod arm
1 mg of mocravimod orally once per day for 12 months
  • Drug: mocravimod
    S1PR modulator
Placebo Comparator
Placebo arm
placebo orally once per day for 12 months
  • Drug: mocravimod
    S1PR modulator

Recruiting Locations

University of Alabama Hospital (UAB Hospital)
Birmingham 4049979, Alabama 4829764 35233-1932
Contact:
Antonio Di Stasi, MD
adistasi@uabmc.edu

Emory University - Winship Cancer Institute (WCI)
Atlanta 4180439, Georgia 4197000 30322-1013
Contact:
Edmund Waller, MD
ewaller@emory.edu

Spectrum Health Medical Group (SHMG) - Blood & Marrow Transplant - Adult (BMT)
Grand Rapids 4994358, Michigan 5001836 49503
Contact:
Sami Brake, MD
Sami.Brake@spectrumhealth.org

University of Rochester Medical Center (URMC)
Rochester 5134086, New York 5128638 14642
Contact:
Eric Huselton, MD
Eric_Huselton@URMC.Rochester.edu

Stony Brook University (SBU) - Cancer Center
Stony Brook 5139865, New York 5128638 11794-0001
Contact:
Fengshuo Lan, MD
Fengshuo.Lan@stonybrookmedicine.edu

The Ohio State University Comprehensive Cancer Center (OSUCCC)
Cleveland 5150529, Ohio 5165418 44106-1716
Contact:
Gabriella Pettito, MD
Gabriella.Pettito@uhhospitals.org

Oregon Health & Science University (OHSU) - Knight Cancer Institute
Portland 5746545, Oregon 5744337 97239-3098
Contact:
Arpita Gandhi, MD
gandhiar@ohsu.edu

University of Pennsylvania - Abramson Cancer Center
Philadelphia 4560349, Pennsylvania 6254927 19104-4206
Contact:
David Porter, MD
david.porter@uphs.upenn.edu

More Details

Status
Recruiting
Sponsor
Priothera SAS

Study Contact

Malika Souquieres, MSc
+33 (0) 6 40 91 26 76
malika.souquieres@priothera.com

Detailed Description

The purpose of this study is to evaluate the efficacy and safety of mocravimod as an adjunctive and maintenance treatment in adult acute myeloid leukemia (AML) patients undergoing allogeneic hematopoietic cell transplantation (HCT).